Medical research

ASH: New approach to gene Tx restores immune cells in X-SCID

(HealthDay)—A new approach to gene therapy can restore immune cell types in infants with newly diagnosed X-linked severe combined immunodeficiency (X-SCID), according to a study presented at the annual meeting of the American ...

Medical research

First non-human primate model for severe combined immunodeficiency

While many insights are gained into diseases and genetic disorders from rodent models, there is a pressing need to find models that can more accurately represent disease progression in the human body, such as non-human primates. ...

Immunology

Gene therapy shows promise for severe combined immunodeficiency

Researchers have found that gene therapy using a modified delivery system, or vector, can restore the immune systems of children with X-linked severe combined immunodeficiency (SCID-X1), a rare, life-threatening inherited ...

Medical research

New gene therapy for 'bubble boy' disease appears effective, safe

A new form of gene therapy for boys with X-linked severe combined immunodeficiency syndrome (SCID-X1), a life-threatening condition also known as "bubble boy" disease, appears to be both effective and safe, according to a ...

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